Scientific discovery driven by genetic diversity
At 澳门正规博彩十大排行平台, we recognize and embrace genetic diversity. Where genomic variation can lead to human disease, our scientists engage in bold and iterative processes of scientific inquiry to provide novel therapies for patients. Our intimate understanding of molecular genetics enables the deliberate and creative design of meaningful therapeutic interventions.
OUR APPROACH
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We are advancing the fundamental understanding of genetic disease.
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Each of our eight approved therapies reset the standard of care for the conditions they treat.
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Each drug candidate we pursue is guided by a fundamental understanding of the genetics and underlying biology of the condition it will address.
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